Treating Muscular Dystrophy with CRISPR Gene Editing
Type
Blog Post
...additional, unique facets of CRISPR DMD therapy. Long et al. show that AAV-CRISPR does not cause obvious germline...directions and obstacles to clinical CRISPR editing
Given the success of the CRISPR-mediated exon skipping approach...To bring DMD CRISPR therapy closer to the clinic, much work is still needed. First, CRISPR delivery must... to be treated clinically with CRISPR. Many obstacles remain for CRISPR gene editing, but given the speed...Resources on Addgene.org
Check out Our CRISPR Guide Pages
Find CRISPR Plasmids for Your Research
Find Validated...Having seen CRISPR’s success in basic research, researchers are eager to apply it in a clinical setting...setting. CRISPR is often used for animal germline modification, to repair or add in disease-causing mutations...