AAV-mediated gene augmentation therapy of CRB1 patient-derived retinal organoids restores the histological and transcriptional retinal phenotype.
Boon N, Lu X, Andriessen CA, Moustakas I, Buck TM, Freund C, Arendzen CH, Bohringer S, Mei H, Wijnholds J
Stem Cell Reports. 2023 May 9;18(5):1123-1137. doi: 10.1016/j.stemcr.2023.03.014. Epub 2023 Apr 20.
(Link opens in a new window)
PubMed
(Link opens in a new window)
Article
Plasmids from Article
No plasmids are currently publicly available from Addgene for this article.