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shRNAs Targeting a Common KCNQ1 Variant Could Alleviate Long-QT1 Disease Severity by Inhibiting a Mutant Allele.

Cocera-Ortega L, Wilders R, Kamps SC, Fabrizi B, Huber I, van der Made I, van den Bout A, de Vries DK, Gepstein L, Verkerk AO, Pinto YM, Tijsen AJ
Int J Mol Sci. 2022 Apr 6;23(7):4053. doi: 10.3390/ijms23074053. (Link opens in a new window) PubMed (Link opens in a new window) Article

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