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Sustained, complete response to pexidartinib in a patient with CSF1R-mutated Erdheim-Chester disease.

Abeykoon JP, Lasho TL, Dasari S, Rech KL, Ranatunga WK, Manske MK, Tischer A, Ravindran A, Young JR, Tobin WO, Flanagan EP, Nowakowski KE, Ruan GJ, Shah MV, Bennani NN, Vassallo R, Ryu JH, Koster MJ, Davidge-Pitts CJ, Patnaik MM, Wu X, Witzig TE, Goyal G, Go RS
Am J Hematol. 2022 Mar 1;97(3):293-302. doi: 10.1002/ajh.26441. Epub 2022 Jan 3. (Link opens in a new window) PubMed (Link opens in a new window) Article

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