CRISPR/Cas9 mediated gene correction ameliorates abnormal phenotypes in spinocerebellar ataxia type 3 patient-derived induced pluripotent stem cells.
He L, Wang S, Peng L, Zhao H, Li S, Han X, Habimana JD, Chen Z, Wang C, Peng Y, Peng H, Xie Y, Lei L, Deng Q, Wan L, Wan N, Yuan H, Gong Y, Zou G, Li Z, Tang B, Jiang H
Transl Psychiatry. 2021 Sep 17;11(1):479. doi: 10.1038/s41398-021-01605-2.
(Link opens in a new window)
PubMed
(Link opens in a new window)
Article
Plasmids from Article
No plasmids are currently publicly available from Addgene for this article.