Allele-specific knockdown of mutant HTT protein via editing at coding region SNP heterozygosities.
Oikemus SR, Pfister E, Sapp E, Chase KO, Kennington LA, Hudgens E, Miller R, Zhu LJ, Chaudhary A, Mick EO, Sena-Esteves M, Wolfe SA, DiFiglia M, Aronin N, Brodsky MH
Hum Gene Ther. 2021 Aug 10. doi: 10.1089/hum.2020.323.
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