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Genome Editing-Mediated Utrophin Upregulation in Duchenne Muscular Dystrophy Stem Cells.

Sengupta K, Mishra MK, Loro E, Spencer MJ, Pyle AD, Khurana TS
Mol Ther Nucleic Acids. 2020 Aug 29;22:500-509. doi: 10.1016/j.omtn.2020.08.031. eCollection 2020 Dec 4. (Link opens in a new window) PubMed (Link opens in a new window) Article

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