Efficient Gene Reframing Therapy for Recessive Dystrophic Epidermolysis Bullosa with CRISPR/Cas9.
Takashima S, Shinkuma S, Fujita Y, Nomura T, Ujiie H, Natsuga K, Iwata H, Nakamura H, Vorobyev A, Abe R, Shimizu H
J Invest Dermatol. 2019 Aug;139(8):1711-1721.e4. doi: 10.1016/j.jid.2019.02.015. Epub 2019 Mar 1.
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