Genome editing in induced pluripotent stem cells rescues TAF1 levels in X-linked dystonia-parkinsonism.
Rakovic A, Domingo A, Grutz K, Kulikovskaja L, Capetian P, Cowley SA, Lenz I, Bruggemann N, Rosales R, Jamora D, Rolfs A, Seibler P, Westenberger A, Konig I, Klein C
Mov Disord. 2018 Jul;33(7):1108-1118. doi: 10.1002/mds.27441.
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