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Engineered AAV capsids mediate transduction of murine neurofibroma and sciatic nerve.

Abou Haidar E, Prabhakar S, Cheah PS, Hanlon KS, Espinoza P, Crain AV, Patel N, Radcliff GW, Cheng M, Hernandez IC, Minderler S, de la Cruz D, Ng C, da Hora CC, Charest A, Stemmer-Rachamimov A, Jowett N, Breakefield XO, Maguire CA
Gene Ther. 2025 Jun 10. doi: 10.1038/s41434-025-00542-9. (Link opens in a new window) PubMed (Link opens in a new window) Article

Plasmids from Article

ID Plasmid Purpose
236254AAV-SC4AAV-SC4 capsid which targets peripheral nerves in mice

Antibodies from Article