Engineered AAV capsids mediate transduction of murine neurofibroma and sciatic nerve.
Abou Haidar E, Prabhakar S, Cheah PS, Hanlon KS, Espinoza P, Crain AV, Patel N, Radcliff GW, Cheng M, Hernandez IC, Minderler S, de la Cruz D, Ng C, da Hora CC, Charest A, Stemmer-Rachamimov A, Jowett N, Breakefield XO, Maguire CA
Gene Ther. 2025 Jun 10. doi: 10.1038/s41434-025-00542-9.
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Plasmids from Article
ID | Plasmid | Purpose |
---|---|---|
236254 | AAV-SC4 | AAV-SC4 capsid which targets peripheral nerves in mice |