AAV Gene Therapy Prevents and Reverses Heart Failure in A Murine Knockout Model of Barth Syndrome.
Wang S, Li Y, Xu Y, Ma Q, Lin Z, Schlame M, Bezzerides VJ, Strathdee D, Pu WT
Circ Res. 2020 Mar 9. doi: 10.1161/CIRCRESAHA.119.315956.
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Plasmids from Article
| ID | Plasmid | Purpose |
|---|---|---|
| 139979 | pCAG/hTAZ-FL | Expresses full length human Tafazzin with codon modified for cloning. Transgene flanked by AAV2 ITR |
| 139980 | pCAG/GFP | expresses GFP under the promoter of CAG. Transgene flanked by AAV2 ITR |
| 139981 | pCAG/Luci | Expresses luciferase under the promoter of CAG. Transgene flanked by AAV2 ITR |