Editing aberrant splice sites efficiently restores beta-globin expression in beta-thalassemia.
Xu S, Luk K, Yao Q, Shen AH, Zeng J, Wu Y, Luo HY, Brendel C, Pinello L, Chui DHK, Wolfe SA, Bauer DE
Blood. 2019 Jan 31. pii: blood-2019-01-895094. doi: 10.1182/blood-2019-01-895094.
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Plasmids from Article
| ID | Plasmid | Purpose |
|---|---|---|
| 114366 | pET-21a_2xNLS_LbCpf1_protein_expression | Protein expression plasmid for 2xNLS LbCpf1 in pET-21a backbone |