Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo.
Yin H, Song CQ, Dorkin JR, Zhu LJ, Li Y, Wu Q, Park A, Yang J, Suresh S, Bizhanova A, Gupta A, Bolukbasi MF, Walsh S, Bogorad RL, Gao G, Weng Z, Dong Y, Koteliansky V, Wolfe SA, Langer R, Xue W, Anderson DG
Nat Biotechnol. 2016 Feb 1. doi: 10.1038/nbt.3471.
(Link opens in a new window)
PubMed
(Link opens in a new window)
Article
Plasmids from Article
| ID | Plasmid | Purpose |
|---|---|---|
| 73451 | J7AAV-HDR Fah.2 | J7AAV-HDR U6sgFah.2 template2 to repair Fah mutation |
| 73452 | J8AAV-HDR Ctnnb1.1 | J8AAV-HDR U6sgCtnnb1.1 template |