Cbh_v5 AAV-ABE C-terminal Citations (8)
Originally described in: Cytosine and adenine base editing of the brain, liver, retina, heart and skeletal muscle of mice via adeno-associated viruses.Levy JM, Yeh WH, Pendse N, Davis JR, Hennessey E, Butcher R, Koblan LW, Comander J, Liu Q, Liu DR Nat Biomed Eng. 2020 Jan;4(1):97-110. doi: 10.1038/s41551-019-0501-5. Epub 2020 Jan 14. PubMed Journal
Articles Citing Cbh_v5 AAV-ABE C-terminal
| Articles |
|---|
| Precise correction of Duchenne muscular dystrophy exon deletion mutations by base and prime editing. Chemello F, Chai AC, Li H, Rodriguez-Caycedo C, Sanchez-Ortiz E, Atmanli A, Mireault AA, Liu N, Bassel-Duby R, Olson EN. Sci Adv. 2021 Apr 30;7(18). pii: 7/18/eabg4910. doi: 10.1126/sciadv.abg4910. Print 2021 Apr. PubMed |
Optimization of base editors for the functional correction of SMN2 as a treatment for spinal muscular atrophy.
Alves CRR, Ha LL, Yaworski R, Sutton ER, Lazzarotto CR, Christie KA, Reilly A, Beauvais A, Doll RM, de la Cruz D, Maguire CA, Swoboda KJ, Tsai SQ, Kothary R, Kleinstiver BP.
Nat Biomed Eng. 2023 Dec 6. doi: 10.1038/s41551-023-01132-z.
PubMed
Associated Plasmids |
| Base editing correction of hypertrophic cardiomyopathy in human cardiomyocytes and humanized mice. Chai AC, Cui M, Chemello F, Li H, Chen K, Tan W, Atmanli A, McAnally JR, Zhang Y, Xu L, Liu N, Bassel-Duby R, Olson EN. Nat Med. 2023 Feb;29(2):401-411. doi: 10.1038/s41591-022-02176-5. Epub 2023 Feb 16. PubMed |
| Single-swap editing for the correction of common Duchenne muscular dystrophy mutations. Chai AC, Chemello F, Li H, Nishiyama T, Chen K, Zhang Y, Sanchez-Ortiz E, Alomar A, Xu L, Liu N, Bassel-Duby R, Olson EN. Mol Ther Nucleic Acids. 2023 Apr 19;32:522-535. doi: 10.1016/j.omtn.2023.04.009. eCollection 2023 Jun 13. PubMed |
| Striated muscle-specific base editing enables correction of mutations causing dilated cardiomyopathy. Grosch M, Schraft L, Chan A, Kuchenhoff L, Rapti K, Ferreira AM, Kornienko J, Li S, Radke MH, Kramer C, Clauder-Munster S, Perlas E, Backs J, Gotthardt M, Dieterich C, van den Hoogenhof MMG, Grimm D, Steinmetz LM. Nat Commun. 2023 Jun 22;14(1):3714. doi: 10.1038/s41467-023-39352-1. PubMed |
| Photoactivatable base editors for spatiotemporally controlled genome editing in vivo. Zou Q, Lu Y, Qing B, Li N, Zhou T, Pan J, Zhang X, Zhang X, Chen Y, Sun SK. Biomaterials. 2023 Nov;302:122328. doi: 10.1016/j.biomaterials.2023.122328. Epub 2023 Sep 13. PubMed |
| CRISPR-Cas9 base editing of pathogenic CaMKIIdelta improves cardiac function in a humanized mouse model. Lebek S, Caravia XM, Straub LG, Alzhanov D, Tan W, Li H, McAnally JR, Chen K, Xu L, Scherer PE, Liu N, Bassel-Duby R, Olson EN. J Clin Invest. 2024 Jan 2;134(1):e175164. doi: 10.1172/JCI175164. PubMed |
| Correction of human nonsense mutation via adenine base editing for Duchenne muscular dystrophy treatment in mouse. Jin M, Lin J, Li H, Li Z, Yang D, Wang Y, Yu Y, Shao Z, Chen L, Wang Z, Zhang Y, Zhang X, Wang N, Xu C, Yang H, Chen WJ, Li G. Mol Ther Nucleic Acids. 2024 Mar 6;35(2):102165. doi: 10.1016/j.omtn.2024.102165. eCollection 2024 Jun 11. PubMed |
If you have published an article using this material, please email us at [email protected] to have your article added to this page.